Therapeutic Peptides Expanded 2 intermediate
Risdiplam: Oligopeptide Research Reference
Risdiplam, a bioactive peptide compound with documented applications in biomedical research, pharmacological studies, and therapeutic development
By Encyclopeptide Editorial | 1 min read
therapeutic-peptides-expanded-2 peptide oligopeptide
Overview
Risdiplam is a bioactive peptide with well-characterized properties and therapeutic applications.
Structure
| Property | Value |
|---|---|
| Name | Risdiplam |
| Sequence | Small molecule SMN2 splicing modifier (pyridazine derivative) |
| Length | Small molecule |
| Molecular Weight | ~372 Da |
| Category | Rare Disease / RNA Splicing Modifier |
Mechanism of Action
Modifies splicing of SMN2 pre-mRNA to increase exon 7 inclusion, raising functional SMN protein levels in motor neurons and peripheral tissues. Oral small molecule alternative to intrathecal nusinersen
References
- Wikipept Peptide Database
- Primary literature (see individual entries)
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